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Dr. Mark Zylka

articles and announcements

Categories: Gene Therapy

Dr. Mark Zylka
December 14, 2019

Validation of therapeutic guide RNAs targeting the UBE3A antisense transcript

Summary of Dr. Zylka Study Dr. Zylka’s lab and others have been exploring the possibility that symptoms associated with Angelman syndrome (AS) can be treated by unsilencing the paternal copy of Ube3a. Dr. Zylka’s lab recently found that paternal Ube3a […]

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